Posts

SRP-9003 rAAVr74.MCK.SCGB Gene Therapy for Limb Girdle Dystrophy (Sarepta Therapeutics): Clinical Study Update

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Gene Therapy for Phenylketonuria: Homology & Biomarin Race to Bring Single Dose Treatment To Market

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Self-Complementary Adeno Associated Virus (scAAV) Vector Design For Efficient Gene Delivery

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CRIM Status, Genotype, Residual Enzyme Activity and Immunogenicity (Unwanted Immune Response)

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Voyager Therapeutics: Overview of Clinical Stage Pipeline

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Gene Therapy for Parkison Disease: RESTORE-1 NBIb-1817 (VY-AADC) Clinical Update

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Gene Therapy for LCA10: The Brilliance Phase 1/2 Clinical Trial Of AGN-151587 (EDIT-101) Update

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Homology Therapeutics, HMI-102 (Gene-therapy) in adult subjects with Phenylketonuria (PKU)

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Targeted Enrichment & Mutation Analysis using Illumina Sequencing Platform (Short Reads ~300 bps)

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T-cell Response After Administration of AVVrh74.MHCK7 For Duchenne Muscular Dystrophy: Result from Open Labeled Control Trial

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Sangamo/Pfizer's Giroctocogene Fitelparvovec Gene Therapy for Hemophilia- Clinical Update

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AAVrh74.MHCK7.micro-dystrophin (Serapta Therapeutics)- SRP- 9001 for Duchenne Muscular: Update From Phase 2 Clinical Studies

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AVV9-minidystrophin (Pfizer- PF-06939926) for Duchenne Muscular Dystrophy: Clinical Study Update

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AAV9- microdystrophin (Solid Biosciences- SGT-001 ) For Duchenne Muscular Dystrophy Treatment: Update on Clinical Studies

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Caribou Biosciences: Overview of Clinical Stage Pipeline

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Homology Medicine: Overview of Clinical Stage Pipeline

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Editas Medicine: Overview of Clinical Stage Pipeline

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Analytical Platform Review: FPLC and UHPLC For Protein Purification and Characterization

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